New Treatment Shows Promising Results In Patients With Duchenne Muscular Dystrophy
A new treatment involving the intramuscular injection of an antisense molecule is safe and effective at increasing the production of the protein dystrophin-the absence of which causes Duchenne muscular dystrophy (DMD). As such, this treatment could benefit a significant proportion of patients with DMD, concludes an Article published Online First and in the October edition of The Lancet Neurology.