Promising New Treatment For Patients With Duchenne Muscular Dystrophy (DMD)

An article published Online First and in the October edition of The Lancet Neurology reports that a new treatment involving the intramuscular injection of an antisense molecule is safe and effective at increasing the production of the protein dystrophin. The absence of this protein causes Duchenne muscular dystrophy (DMD). This treatment could help a considerable proportion of patients with DMD.